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Vitravene: how long were the pivotal tox studies?

fomivirsen · CMV IE2 mRNA (ASO)
Longest pivotal study
13 weeks
“No intact fomivirsen was observed in any of tissues (kidney, liver, ovary, and uterus) following 1, 3, or 8 doses of 10 uM (115 ug) fomivirsen administered every-other-week for three months.”
✓ VerifiedFDA review, p. 33Source ↗
Pivotal GLP studies
Cynomolgus monkey multiple-dose intravitreal ocular toxicity and systemic exposure study, with prophylactic corticosteroid
“To evaluate the effects of ISIS 2922 on ocular tissues in cynomolgus monkeys that have received prophylactic corticosteroid treatment and to determine the systemic exposure (i.e. plasma, kidney, liver, and uterus concentrations) following multiple intravitreal injection.”
✓ VerifiedFDA review, p. 23Source ↗
Route in tox
Intravitreal
“Ocular kinetic parameters of fomivirsen following intravitreal injection to rabbits and monkeys are summarized in the following table.”
✓ VerifiedFDA review, p. 32Source ↗

Same question, other oligonucleotides

Amvuttra

vutrisiran · TTR (siRNA)
40 weeks

Cyfendus

anthrax vaccine adsorbed, adjuvanted · TLR9 (CpG 7909 adjuvant)
4 (adult rat repeat-dose study, full human dose on SD 1, 15, 29)

Dawnzera

donidalorsen · Prekallikrein / KLKB1 (ASO)
39 weeks

Defitelio

defibrotide · Fragmented DNA oligonucleotides
13 weeks

Givlaari

givosiran · ALAS1 (siRNA)
39 weeks

Heplisav-B

hepatitis B vaccine (recombinant), adjuvanted · TLR9 (CpG 1018 adjuvant)
8 (rat and cynomolgus monkey, weekly SC CpG 1018 alone)

Izervay

avacincaptad pegol · C5 (aptamer)
39 weeks

Kynamro

mipomersen · APOB (ASO)
52 weeks

Leqvio

inclisiran · PCSK9 (siRNA)
40 weeks

Macugen

pegaptanib · VEGF-165 (aptamer)
39 weeks

Onpattro

patisiran · TTR (siRNA)
39 weeks

Oxlumo

lumasiran · HAO1 (siRNA)
36 weeks

Qalsody

tofersen · SOD1 (ASO)
39 weeks

Qfitlia

fitusiran · Antithrombin / SERPINC1 (siRNA)
39 weeks

Redemplo

plozasiran · APOC3 (siRNA)
37 weeks

Rivfloza

nedosiran · LDHA (siRNA)
39 weeks

Rytelo

imetelstat · Telomerase (oligo)
39 weeks

Spinraza

nusinersen · SMN2 (ASO)
53 weeks

Tegsedi

inotersen · TTR (ASO)
39 weeks

Viltepso

viltolarsen · DMD exon 53 (PMO)
39 weeks

Wainua

eplontersen · TTR (ASO)
39 weeks

Waylivra

volanesorsen · APOC3 (ASO)
39 weeks

Summary across all 28 oligonucleotides →